Articles tagged with “orphan-drugs”

Rare Diseases in 2025: Diagnosis, Treatment & Policy

Explore the 2025 rare disease landscape, affecting 300 million people globally. Learn about diagnostic challenges, orphan drug development, and future policy di

135 min read

11/15/2025

rare diseases orphan drugs genetic disorders diagnostic odyssey public health drug development gene therapy

Most Expensive Drugs in the US: A 2025 Price List

See the 2025 list of the most expensive drugs in the USA, led by multi-million dollar gene therapies like Lenmeldy & Elevidys for rare diseases. Learn why price

10 min read

10/8/2025

drug pricing gene therapy orphan drugs rare diseases lenmeldy elevidys pharmacoeconomics biotechnology