Vertex Pharmaceuticals

Vertex Pharmaceuticals is a global biotechnology company that invests in scientific innovation to create transformative medicines for people with serious diseases. The company is the undisputed leader in the treatment of cystic fibrosis (CF), with a portfolio of four approved medicines that treat the underlying cause of the disease for the vast majority of patients globally. Beyond CF, Vertex is rapidly diversifying its portfolio into other high-value therapeutic areas including sickle cell disease, beta thalassemia, acute and neuropathic pain, and inflammatory kidney diseases. The company is known for its 'rational drug design' approach, focusing on targets with clear biological validation and high unmet medical need.