uniQure N.V.

uniQure is a biopharmaceutical company focused on the development of transformative gene therapies for patients with serious unmet medical needs. The company leverages a proprietary adeno-associated virus (AAV) gene therapy platform to create one-time, potentially curative treatments for genetic and other devastating diseases. Headquartered in Amsterdam, Netherlands, with significant operations in Lexington, Massachusetts, uniQure has established itself as a pioneer in the gene therapy space. The company is known for its internal R&D capabilities and its strategic manufacturing facility, which allows it to maintain control over the production of its complex gene therapy products.